Clin Exp Pediatr.
2020 Jan;63(1):14-15. 10.3345/kjp.2018.07402.
Considerations for evaluating the effectiveness and long-term outcome of enzyme replacement therapy in Pompe disease
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- 1Department of Pediatrics, Pusan National University Children’s Hospital, Yangsan, Korea
- KMID: 2502852
- DOI: http://doi.org/10.3345/kjp.2018.07402
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